4項罕見疾病藥物於「新藥及新醫材病友意見分享」平台蒐集意見,病友可至平台填寫。
2023/2/10
一、罕見疾病藥物
(1)EVRYSDI Powder for Oral Solution 0.75mg/ml
(2)Luxturna concen trate and solvent for solution for injection
(3)Uplizna for Intraven ous Infusion 100mg
(4)ZOLGENSMA Suspension for Intravenous Infusion